Defining phenotype, tropism, and retinal gene therapy using adeno-associated viral vectors (AAVs) in new-born brown norway rats with a spontaneous mutation in CRB1CRB2 Loss in Rod Photoreceptors Is Associated with Progressive Loss of Retinal Contrast SensitivityHuman iPSC-Derived Retinas Recapitulate the Fetal CRB1 CRB2 Complex Formation and Demonstrate that Photoreceptors and Müller Glia Are Targets of AAV5CRB1 is required for recycling by RAB11A+ vesicles in human retinal organoidsLoss of CRB2 in Müller glial cells modifies a CRB1-associated retinitis pigmentosa phenotype into a Leber congenital amaurosis phenotype
author
type
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Carolina R Jost
firstName
Carolina R