Characterizing responses to CFTR-modulating drugs using rectal organoids derived from subjects with cystic fibrosisRectal Organoids Enable Personalized Treatment of Cystic FibrosisSensitive Monogenic Noninvasive Prenatal Diagnosis by Targeted HaplotypingCRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid BiobankForskolin-induced swelling of intestinal organoids correlates with disease severity in adults with cystic fibrosis and homozygous F508del mutationsStratifying infants with cystic fibrosis for disease severity using intestinal organoid swelling as a biomarker of CFTR function
author
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Evelien Kruisselbrink
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Kruisselbrink